Stuart Orkin

Stuart H. Orkin
Born (1946-04-23) April 23, 1946
Manhattan, New York, U.S.
Alma materMassachusetts Institute of Technology (B.S.)
Harvard Medical School (M.D.)
Known forMolecular genetics of blood disorders;
GATA transcription factors;
BCL11A and fetal hemoglobin regulation;
CRISPR/Cas9 gene editing therapy (Casgevy) for sickle cell disease
AwardsE. Mead Johnson Award (1987)
Warren Alpert Foundation Prize (1993)
Jessie Stevenson Kovalenko Medal (2013)
William Allan Award (2014)
George M. Kober Medal (2018)
Nemmers Prize (2018)
King Faisal Prize (2020)
Gruber Prize in Genetics (2021)
Canada Gairdner International Award (2022)
Shaw Prize (2024)
Scientific career
FieldsHematology, Pediatric oncology, Stem cell biology
InstitutionsBoston Children's Hospital
Dana–Farber Cancer Institute
Harvard Medical School
Academic advisorsPhilip Leder
Notable studentsJean-Pierre Bourquin

Stuart Holland Orkin (born April 23, 1946) is an American physician-scientist specializing in hematology, pediatric oncology, and stem cell biology. He is the David G. Nathan Distinguished Professor of Pediatrics at Harvard Medical School and an Investigator of the Howard Hughes Medical Institute (HHMI) at Boston Children's Hospital. Orkin is known for defining the molecular basis of human blood disorders, discovering key hematopoietic transcription factors, and pioneering gene therapy and gene editing approaches for sickle cell disease and thalassemia. He is a member of the National Academy of Sciences and the Institute of Medicine.